Potential therapies

Drug Development Pipeline for Myotonic Dystrophy Type 1 (DM1) and Myotonic Dystrophy Type 2 (DM2)

Below is a pipeline of potential therapies for myotonic dystrophy being developed by pharmaceutical companies, hospitals and universities. The table includes therapies in early laboratory development all the way up to early and late clinical development.

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This information is accurate as of 30/04/20. This was initially based on the work of Nate Uhl at www.myotonicpipeline.com. Nate can be contacted at nateuhl.please.remove@yahoo.com or on his twitter page: @DM1research

If you have any questions do not hesitate to contact the registry curator at: myotonicdystrophyregistry@treat-nmd.org